Volunteer Story: Victoria and Julia (Niemann-Pick Disease Type C)

Volunteer Story: Victoria and Julia (Niemann-Pick Disease Type C)

Niemann-Pick disease type C, or NPC, is a rare childhood disease that gradually impairs brain function and movement. Researchers at the 2023 ÃÛÑ¿´«Ã½ conduct NPC research, including clinical trials that test promising therapies.

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